Cyrus Bascon
Sr. CRC
Pediatrics
School of Medicine

Publications (1)

Top publication keywords:
Child, PreschoolHumansMale2-Hydroxypropyl-beta-cyclodextrinInfantRetrospective StudiesChildFemaleNiemann-Pick Disease, Type CYoung AdultAdolescentAdult

• Expanded access with intravenous hydroxypropyl-β-cyclodextrin to treat children and young adults with Niemann-Pick disease type C1: a case report analysis.
  Orphanet journal of rare diseases 2019 Hastings C, Vieira C, Liu B, Bascon C, Gao C, Wang RY, Casey A, Hrynkow S